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SPINAL 
MUSCULAR 
ATROPHY
DISEASE MECHANISMS AND THERAPY
Edited by
Charlotte J. Sumner
Johns Hopkins University School of Medicine, Baltimore, MD, United States
Sergey PauShkin
Spinal Muscular Atrophy (SMA) Foundation, New York, NY, United States
Chien-Ping ko
University of Southern California, Los Angeles, CA, United States
AMSTERDAM • BOSTON • HEIDELBERG • LONDON 
NEW YORK • OXFORD • PARIS • SAN DIEGO 
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Academic Press is an imprint of Elsevier
	SPINAL MUSCULAR ATROPHY: DISEASE MECHANISMS AND THERAPY